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More Than 95% of Rare Diseases Have No Treatment. Clinical Trials Are Essential for Identifying Therapeutic Options ... Participating in a clinical trial can help ...
May 5, 2023 · The traditional clinical trial with fixed treatment groups can be ill suited to rare diseases, with some researchers opting for adaptive trials.
Pfizer's clinical research in rare diseases focuses on developing new medicines or therapies such as gene therapy. Explore rare disease clinical trials.
Recruit rare disease clinical trial patients. Finding the right patient for your rare disease trial can be a challenge. PPD offers flexible, innovative ...
The Rare Diseases Clinical Research Network (RDCRN) program is designed to advance medical research on rare diseases by providing support for clinical studies ...
We oversee this NIH-wide program that supports medical research on over 200 rare diseases through clinical studies, including collaborations, study enrollment ...
Pfizer has an unwavering commitment to ethical and quality rare disease research and new drug pipeline. Find a Pfizer rare disease clinical trial.
Feb 22, 2024 · Clinical innovation in rare diseases requires deep expertise and close collaboration across multiple groups, including with patient communities, ...
Dec 13, 2022 · The inherently small population of patients with a rare disease can also make conducting clinical trials difficult. Since the Orphan Drug ...